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Lung SORT LNPs enable precise homology-directed repair mediated CRISPR/Cas genome correction in cystic fibrosis models.

Nov 13, 2023

ABOUT THE CONTRIBUTORS

  • Tuo Wei

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Yehui Sun

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Qiang Cheng

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Sumanta Chatterjee

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Zachary Traylor

    Department of Genetics and Genome Sciences, Case Western Reserve University School of Medicine, Cleveland, OH, USA.

    Department of Pediatrics, Case Western Reserve University School of Medicine, Cleveland, OH, USA.

    Lindsay T Johnson

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Melissa L Coquelin

    ReCode Therapeutics, Menlo Park, CA, USA.

    Jialu Wang

    ReCode Therapeutics, Menlo Park, CA, USA.

    Michael J Torres

    ReCode Therapeutics, Menlo Park, CA, USA.

    Xizhen Lian

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Xu Wang

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Yufen Xiao

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA.

    Craig A Hodges

    Department of Genetics and Genome Sciences, Case Western Reserve University School of Medicine, Cleveland, OH, USA.

    Department of Pediatrics, Case Western Reserve University School of Medicine, Cleveland, OH, USA.

    Daniel J Siegwart

    Department of Biomedical Engineering, Program in Genetic Drug Engineering, The University of Texas Southwestern Medical Center, Dallas, TX, USA. Daniel.Siegwart@UTSouthwestern.edu.

    Department of Biochemistry, The University of Texas Southwestern Medical Center, Dallas, TX, USA. Daniel.Siegwart@UTSouthwestern.edu.

    Simmons Comprehensive Cancer Center, The University of Texas Southwestern Medical Center, Dallas, TX, USA. Daniel.Siegwart@UTSouthwestern.edu.

REFERENCES & ADDITIONAL READING

PubMed

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